A new generation of therapies are transforming treatment of human genetic disease. These gene-centered approaches—gene editing, gene therapy, mRNA replacement, oligonucleotide therapy, and related approaches—represent a significant new and rapidly growing sector in biomedical research that will transform healthcare. Development of these therapies requires dedicated pipelines to translate basic research into treatments for patients.
FIND Pipeline is leading the way with tools to advance gene-centered therapeutics into clinical trials. Our integrated operation bridges candidate therapeutics from the bench to the patient and back. Our tools and services are widely used by academic and commercial researchers and physicians in Northeast Ohio and around the world. The small number of patients for many genetic diseases poses a challenge for advancement through clinical trials. Strong preclinical data in support of in vivo safety and efficacy are needed.